Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Development of a target concentration intervention to individualize paroxysmal nocturnal hemoglobinuria treatment with pegcetacoplan Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Patients' perspectives on oral decitabine/cedazuridine for the treatment of myelodysplastic syndromes/neoplasms Therapeutic Advances in Hematology Myelodysplastic Syndromes (MDS)
Improvements in hematologic markers and decreases in fatigue with pegcetacoplan for patients with paroxysmal nocturnal hemoglobinuria and mild or moderate anemia (hemoglobin ≥10 g/dL) who had received eculizumab or were naive to complement inhibitors PLOS One Paroxysmal Nocturnal Hemoglobinuria (PNH)
Luspatercept versus epoetin alfa in erythropoiesis-stimulating agent-naive, transfusion-dependent, lower-risk myelodysplastic syndromes (COMMANDS): primary analysis of a phase 3, open-label, randomised, controlled trial Lancet Hematology Myelodysplastic Syndromes (MDS)
A stimulating advance in erythropoiesis for patients with myelodysplastic syndromes Lancet Haematology Myelodysplastic Syndromes (MDS)
Low dose lenalidomide versus placebo in non-transfusion dependent patients with low risk, del(5q) myelodysplastic syndromes (SintraREV): a randomised, double-blind, phase 3 trial Lancet Haematology Myelodysplastic Syndromes (MDS)
Alternative donor transplantation for severe aplastic anemia: a comparative study of the SAAWP EBMT Blood Aplastic Anemia
Paroxysmal nocturnal hemoglobinuria-related thrombosis in the era of novel therapies: a 2043-patient-year analysis Blood Paroxysmal Nocturnal Hemoglobinuria (PNH)
Childhood myelodysplastic syndromes: Is cytoreductive therapy useful before allogeneic hematopoietic stem cell transplantation? HemaSphere Myelodysplastic Syndromes (MDS)
Molecular Taxonomy of Myelodysplastic Syndromes and its Clinical Implications Blood Myelodysplastic Syndromes (MDS)

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