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Kidney involvement in myelodysplastic syndromes |
Jun 2024 |
Clinical Kidney Journal |
Myelodysplastic Syndromes (MDS) |
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Phase 3 randomized COMMODORE 2 trial: Crovalimab versus eculizumab in patients with paroxysmal nocturnal hemoglobinuria naive to complement inhibition |
Jun 2024 |
American Journal of Hematology |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Acquired Aplastic Anemia Therapies: Immunosuppressive Therapy Versus Alternative Donor Hematopoietic Cell Transplantation |
Jun 2024 |
Journal of Hematology |
Aplastic Anemia |
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Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria |
Jun 2024 |
Blood Advances |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria |
Jun 2024 |
The New England Journal of Medicine |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria. Reply |
Jun 2024 |
The New England Journal of Medicine |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria |
Jun 2024 |
The New England Journal of Medicine |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
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Haploidentical stem cell transplantation (haplo-SCT) represents the main alternative for children with inherited bone marrow failure syndrome (I-BMF) lacking a matched donor. This retrospective study, conducted on behalf of the EBMT SAAWP and PDWP, aims t |
Jun 2024 |
American Society of Clinical Oncology Educational Book |
Myelodysplastic Syndromes (MDS) |
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HLA-haploidentical stem cell transplantation in children with inherited bone marrow failure syndromes: A retrospective analysis on behalf of EBMT severe aplastic Anemia and pediatric diseases working parties |
Jun 2024 |
American Journal of Hematology |
Aplastic Anemia |
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Iptacopan and danicopan for paroxysmal nocturnal hemoglobinuria |
Jun 2024 |
Journal of Managed Care & Specialty Pharmacy |
Paroxysmal Nocturnal Hemoglobinuria (PNH) |
