Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Clonal Hematopoiesis, Inflammation, and Hematologic Malignancy Annual Review of Pathology: Mechanisms of Disease Aplastic Anemia, Myelodysplastic Syndromes (MDS), Paroxysmal Nocturnal Hemoglobinuria (PNH)
Predictors for improvement in patient-reported outcomes: post hoc analysis of a phase 3 randomized, open-label study of eculizumab and ravulizumab in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Deciphering treatment patterns in non-severe/moderate aplastic anemia: an international observational study Leukemia Aplastic Anemia
Patterns of Diagnostic Evaluation and Determinants of Treatment in Older Patients With Non-transfusion Dependent Myelodysplastic Syndromes Oncologist Myelodysplastic Syndromes (MDS)
Eltrombopag for Low-Risk Myelodysplastic Syndromes With Thrombocytopenia: Interim Results of a Phase II, Randomized, Placebo-Controlled Clinical Trial (EQOL-MDS) Journal of Clinical Oncology Myelodysplastic Syndromes (MDS)
A Journey from Blood Cells to Genes and Back Annual Review of Genomics and Human Genetics Paroxysmal Nocturnal Hemoglobinuria (PNH)
Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Factor B inhibitor iptacopan for the treatment of paroxysmal nocturnal hemoglobinuria Blood Reviews Paroxysmal Nocturnal Hemoglobinuria (PNH)
Efficacy and safety of the C5 inhibitor crovalimab in complement inhibitor-naive patients with PNH (COMMODORE 3): A multicenter, Phase 3, single-arm study American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Transplantation Referral Patterns for Patients with Newly Diagnosed Higher-Risk Myelodysplastic Syndromes and Acute Myeloid Leukemia at Academic and Community Sites in the Connect® Myeloid Disease Registry: Potential Barriers to Care Transplantation and Cellular Therapy Myelodysplastic Syndromes (MDS)

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