Filgrastim
It is known as a hematopoietic growth factor growth factor: A substance made by the body that stimulates the bone marrow to produce blood cells.
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Eculizumab
Eculizumab Eculizumab: Eculizumab (Soliris ®) is given as an IV into a vein at the doctor’s office or at a special center. The procedure usually takes about 35 minutes.
Deferiprone
Deferiprone Deferiprone: Deferiprone is in a class of medications called iron chelators.
Deferasirox
It comes in a tablet form which is dissolved in juice or water and taken by mouth. Iron build-up can occur in patients who get a lot of red blood cell red blood cell: The most
Cyclosporine
Cyclosporine Cyclosporine: Cyclosporine is used along with antithymocyte globulin (ATG), another immunosuppressant, for treating aplastic anemia and some other forms of bone marrow failure
Antithymocyte Globulin
ATG is an immunosuppressant, a drug that lowers the body's immune response.
Fund Your Research
AAMDSIF advocates for and invests in collaborative research to accelerate the discovery of better treatments and cures for bone marrow failure disorders.
AAMDSIF Research Grants
Know Your Treatment Options
Caring for Yourself
[[nid:147 filter=intro]]
Therapies
[[nid:4376 filter=intro]]
Bone Marrow Transplants
[[nid:4345 filter=intro]]
Clinical Trials
[[nid:634 filter=intro]]
Peer Support Network
Connecting with other patients and families can be a powerful and uplifting experience. Our networks let you learn from others, share your journey, get and give support and make new friends. You have the option of connecting on a one-to-one basis or with a group. You also choose the way you prefer to interact - by phone, in person or online.
Patient and Family HelpLine
You are not alone. The AAMDSIF HelpLine has trained and compassionate information specialists ready to answer your questions and provide the support you need. To speak with an information specialist, please call (800) 747-2820, option 2, or email help@aamds.org.