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Aplastic Anemia - 2025 Kansas City Patient and Family Conference

Topic(s)

Aplastic Anemia

Presenter(s)

Taha Bat, MD

In this recording, Dr. Taha Bat discusses the diagnosis of aplastic anemia along with treatment options for patients. Recording includes the question-and-answer session.

Reduced venetoclax exposure to 7 days vs standard exposure with hypomethylating agents in newly diagnosed AML patients

Original Publication Date

April 17, 2025

Article Source

External Web Content

Abstract Hypomethylating agent (HMA) plus venetoclax (VEN) regimens are standard of care in patients with acute myeloid leukemia (AML) ineligible for intensive chemotherapy. While the VEN label recommends continuous 28-day cycles, shortened VEN durations may induce similar…

Cell-autonomous dysregulation of interferon signaling drives clonal expansion of SRSF2-mutant MDS stem/progenitor cells

Original Publication Date

March 31, 2025

Article Source

External Web Content

Key Points SRSF2 mutations blunt responsiveness of MDS cells to IFN stimulation and promote their clonal fitness by downregulating STAT1 expression Proteasome inhibition restores STAT1 protein level and sensitivity of SRSF2-mutant MDS cells to IFN, suggesting a new therapeutic…

Natural killer cells’ functional impairment drives the immune escape of pre-malignant clones in early-stage myelodysplastic syndromes

Original Publication Date

April 11, 2025

Article Source

External Web Content

Abstract Dissecting the preneoplastic disease states’ biological mechanisms that precede tumorigenesis can lead to interventions that can slow down disease progression and/or mitigate disease-related comorbidities. Myelodysplastic syndromes (MDS) cannot be cured by currently…

2025 Boston Patient and Family Conference

Read more about 2025 Boston Patient and Family Conference

Session Recordings Available:

MDS to MPN Overlap from the 2025 Boston Patient and Family Conference

High Risk MDS from the 2025 Boston Patient and Family Conference

Low Risk MDS from the 2025 Boston Patient and Family Conference

2025 Chapel Hill Patient and Family Conference

Read more about 2025 Chapel Hill Patient and Family Conference

Recordings:

March for Marrow: Walk for PNH NJ / NY

Read more about March for Marrow: Walk for PNH NJ / NY

Join us in Verona Park, NJ on Sunday, September 28, 2025 for a day of remembrance and awareness in celebration of the 19th Annual Walk for PNH.

The Walk for PNH is the nation's largest event to raise awareness and funds for PNH education and research. This inspiring event calls on participants of all ages and abilities to join in the fight against PNH.

AAMDSIF Joins Coalition Urging the Administration to Preserve our Nation’s Newborn Screening Program

Original Publication Date

May 6, 2025

Article Source

Coalition Action

A coalition of 272 organizations signed a public letter to the Secretary, Department of Health and Human Services, addressing the decision to eliminate the Advisory Committee on Heritable Disorders in Newborns and Children (ACHDNC). While each state may add on additional…

Judy's Story of PNH - Always Moving Forward - 2025 Kansas City Patient and Family Conference

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Topic(s)

Paroxysmal Nocturnal Hemoglobinuria (PNH)

Judy talks about her PNH journey from diagnosis, treatment decisions and moving forward.

PNH and Current Therapies - from the 2025 Kansas City Patient and Family Conference

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Topic(s)

Paroxysmal Nocturnal Hemoglobinuria (PNH)

Presenter(s)

Srinivasa Reddy Sanikommu, MD

In this recording, Dr. Srinivasa Sanikommu discusses current thinking on PNH and therapies that are available to patients. Recording includes the question-and-answer session.

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Aplastic Anemia - 2025 Kansas City Patient and Family Conference

Reduced venetoclax exposure to 7 days vs standard exposure with hypomethylating agents in newly diagnosed AML patients

Cell-autonomous dysregulation of interferon signaling drives clonal expansion of SRSF2-mutant MDS stem/progenitor cells

Natural killer cells’ functional impairment drives the immune escape of pre-malignant clones in early-stage myelodysplastic syndromes

2025 Boston Patient and Family Conference

2025 Chapel Hill Patient and Family Conference

March for Marrow: Walk for PNH NJ / NY

AAMDSIF Joins Coalition Urging the Administration to Preserve our Nation’s Newborn Screening Program

Judy's Story of PNH - Always Moving Forward - 2025 Kansas City Patient and Family Conference

PNH and Current Therapies - from the 2025 Kansas City Patient and Family Conference

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