Instructions
If you are interested in learning more about your possible participation in this clinical trial, please complete the form. Your information will be forwarded directly to the sponsoring company.
Status:
Recruiting
Phase:
Phase 2
Gender:
Female
Male
Age Group:
3 years and older
Accepts Healthy Volunteers:
No
Inclusion Criteria:
Eligible participants:
- Are 3 and older (minors must have parent/guardian consent to participate);
- Are diagnosed with a short telomere disease;
- Also have abnormalities affecting the bone marrow such as aplastic anemia or low blood counts OR lung disease OR liver disease.
Exclusion Criteria:
Personal history of bone marrow transplant.