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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Modified Delphi panel consensus recommendations for management of severe aplastic anemia Aug 2024 Blood Advances Aplastic Anemia
Hemolysis events in the Phase 3 PEGASUS study of pegcetacoplan in patients with paroxysmal nocturnal hemoglobinuria Apr 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
DNA methylation identifies genetically and prognostically distinct subtypes of myelodysplastic syndromes Oct 2019 Blood Advances Myelodysplastic Syndromes (MDS)
Glasdegib as maintenance therapy for patients with AML and MDS patients at high risk for postallogeneic stem cell transplant relapse Jul 2020 Blood Advances Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Long-term efficacy and safety of romiplostim in refractory aplastic anemia: follow-up of a phase 2/3 study Dec 2023 Blood Advances Aplastic Anemia
Health-Related Quality of Life and Vulnerability among People with Myelodysplastic Syndromes: A US National Study May 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Jun 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Activity of luspatercept and ESAs combination for treatment of anemia in lower-risk myelodysplastic syndromes Jul 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Health-related quality of life and vulnerability among people with myelodysplastic syndromes: a US national study Jul 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Pegcetacoplan controls hemolysis in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Jun 2023 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)