Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
RNA splicing as a therapeutic target in myelodysplastic syndromes Seminars in Hematology Myelodysplastic Syndromes (MDS)
Crovalimab in the paroxysmal nocturnal hemoglobinuria treatment landscape Immunotherapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Targeted therapies for myelodysplastic syndromes/neoplasms (MDS): current landscape and future directions Expert Review of Anticancer Therapy Myelodysplastic Syndromes (MDS)
Terminal complement inhibition and control of hemolysis in patients with paroxysmal nocturnal hemoglobinuria who switched from high-dose eculizumab to ravulizumab: a phase IV, single-arm clinical trial Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Supportive care strategies in myelodysplastic syndromes and acute myeloid leukemia in older adults: a national survey of Canadian hematologists Annals of Hematology Myelodysplastic Syndromes (MDS)
Health-related quality of life and symptom-specific functional impairment among patients treated with parenterally administered complement inhibitors for paroxysmal nocturnal hemoglobinuria Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Real-world impact of luspatercept on red blood cell transfusions among patients with myelodysplastic syndromes: A United States healthcare claims database study Leukemia Research Myelodysplastic Syndromes (MDS)
Clinical and neurophysiological aspects of peripheral neuropathy in patients with myelodysplastic syndromes British Journal of Haematology Myelodysplastic Syndromes (MDS)
Sustained benefits of imetelstat on patient-reported fatigue in patients with lower-risk myelodysplastic syndromes ineligible for, or relapsed/refractory to, erythropoiesis-stimulating agents and high transfusion burden in the phase 3 IMerge study Leukemia & Lymphoma Myelodysplastic Syndromes (MDS)
Consensus recommendations for severe aplastic anemia Blood Advances Aplastic Anemia

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