Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
T-cell dysfunctions in myelodysplastic syndromes Blood Myelodysplastic Syndromes (MDS)
Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study Advances in Therapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Luspatercept in low-risk myelodysplastic syndromes: a paradigm shift in treatment strategies Expert Opinion on Biological Therapy Myelodysplastic Syndromes (MDS)
Expert consensus on the management of pharmacodynamic breakthrough-hemolysis in treated paroxysmal nocturnal hemoglobinuria Hematology. Paroxysmal Nocturnal Hemoglobinuria (PNH)
SOHO State of the Art Updates and Next Questions: An Update on Higher Risk Myelodysplastic Syndromes Clinical Lymphoma, Myeloma & Leukemia Myelodysplastic Syndromes (MDS)
Oral Iptacopan Monotherapy in Paroxysmal Nocturnal Hemoglobinuria The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal nocturnal hemoglobinuria: Review of the patient experience and treatment landscape Blood Reviews Paroxysmal Nocturnal Hemoglobinuria (PNH)
Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Understanding pharmacological complement inhibition in paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Current use of androgens in bone marrow failure disorders: a report from the Severe Aplastic Anemia Working Party of the European Society for Blood and Marrow Transplantation Haematologica Aplastic Anemia

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