Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Efficacy and Safety of Inhibitors of the Proximal Pathway of the Complement System in Paroxysmal Nocturnal Hemoglobinuria: A Meta-analysis of Randomized Controlled Trials American Journal of Therapeutics Paroxysmal Nocturnal Hemoglobinuria (PNH)
Targeted therapies for myelodysplastic syndromes/neoplasms (MDS): current landscape and future directions Expert Review of Anticancer Therapy Myelodysplastic Syndromes (MDS)
Iptacopan for the treatment of paroxysmal nocturnal hemoglobinuria Expert Opinion on Pharmacotherapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Iptacopan for the treatment of paroxysmal nocturnal hemoglobinuria Expert Opinion on Pharmacotherapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Massive hemolysis in paroxysmal nocturnal hemoglobinuria after switching from proximal complement inhibitor to anti-C5 therapy: A lesson not to be forgotten American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Family reflections: pediatric aplastic anemia research; a parent perspective Pediatric Research Aplastic Anemia, Pediatric
Cost-effectiveness of iptacopan for paroxysmal nocturnal hemoglobinuria Blood Paroxysmal Nocturnal Hemoglobinuria (PNH)
Myelodysplastic Syndromes Treatment (PDQ®): Patient Version PDQ Cancer Information Summaries Myelodysplastic Syndromes (MDS)
Advances in the management of higher-risk myelodysplastic syndromes: future prospects Leukemia & Lymphoma Myelodysplastic Syndromes (MDS)
Luspatercept versus epoetin alfa in erythropoiesis-stimulating agent-naive, transfusion-dependent, lower-risk myelodysplastic syndromes (COMMANDS): primary analysis of a phase 3, open-label, randomised, controlled trial The Lancet Haematology Myelodysplastic Syndromes (MDS)

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