Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Outcomes of patients with higher-risk myelodysplastic syndromes/neoplasms treated with hypomethylating agents + venetoclax-an analysis from the International Consortium for MDS (icMDS) VALIDATE database Blood Cancer Journal Myelodysplastic Syndromes (MDS)
Immunological links between aplastic anemia and paroxysmal nocturnal hemoglobinuria International Journal of Hematology Aplastic Anemia
Iptacopan monotherapy resulted in increased hemoglobin level in patients with PNH and hemoglobin ≥10 g/dL after anti-C5 therapy HemaSphere Paroxysmal Nocturnal Hemoglobinuria (PNH)
Iptacopan monotherapy resulted in increased hemoglobin level in patients with PNH and hemoglobin ≥10 g/dL after anti-C5 therapy HemaSphere Paroxysmal Nocturnal Hemoglobinuria (PNH)
A Survey of Provider Practices for Diagnosis and Treatment of Pediatric Moderate Aplastic Anemia From the North American Pediatric Aplastic Anemia Consortium Journal of Pediatric Hematology/Oncology (JPHO) Aplastic Anemia
Clonal Dynamics of Hematopoiesis in Aplastic Anemia after Immunosuppression and Eltrombopag The New England Journal of Medicine Aplastic Anemia
Clonal Selection and Evolution after Treatment of Severe Aplastic Anemia The New England Journal of Medicine Aplastic Anemia
High-resolution single-cell mapping of clonal hematopoiesis and structural variation in aplastic anemia Nature Genetics Aplastic Anemia
Clonal Hematopoiesis Diversity in Aplastic Anemia - When Does It Matter Clinically? The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Real-World Effectiveness and Safety of Ravulizumab in Patients With Paroxysmal Nocturnal Hemoglobinuria: Evidence From the International PNH Registry American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)

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