treatment

SOLIRIS Fact Sheet

SOLIRIS is a prescription medicine called a monoclonal antibody. SOLIRIS is used to treat adults with a disease called Paroxysmal Nocturnal Hemoglobinuria (PNH)

VOYDEYA Fact Sheet

VOYDEYA is a prescription medicine used along with ravulizumab or eculizumab to treat breakdown of red blood cells that takes place outside of blood vessels (extravascular hemolysis), in adults with paroxysmal nocturnal…

ULTOMIRIS Fact Sheet

ULTOMIRIS® is a prescription medicine called a monoclonal antibody. ULTOMIRIS® is used to treat adults and children 1 month of age and older with a disease called Paroxysmal Nocturnal Hemoglobinuria (PNH)

VENCLEXTA Fact Sheet

Venclexta® (also known as Venetoclax) is a prescribed oral tablet approved by the Food and Drug Administration for adult patients with acute myeloid leukemia (AML)

RYTELO Fact Sheet

RYTELO (imetelstat) is an oligonucleotide telomerase inhibitor used to treat adults with IPSS-R low to intermediate-1 myelodysplastic syndromes (MDS) with transfusion dependent anemia requiring four or more red blood…

TIBSOVO Fact Sheet

TIBSOVO is a prescribed medication approved to treat adult patients with myelodysplastic syndromes (MDS) with an isocitrate dehydrogenase-1 (IDH1) mutation either when the disease has relapsed or has not improved after…

REBLOZYL Fact Sheet

REBLOZYL® (luspatercept-aamt) was the first erythroid maturation agent (EMA) approved in 2020 by the Food and Drug Administration for the treatment of anemia in adult patients with myelodysplastic syndromes (MDS) who…

INQOVI Fact Sheet

INQOVI® (previously known as ASTX727) is a prescribed oral tablet combination of decitabine and cedazuridine approved by the Food and Drug Administration for adult patients with myelodysplastic syndromes (MDS) and…

FABHALTA Fact Sheet

FABHALTA, a complement factor B inhibitor, is the first oral medication approved to treat adults with paroxysmal nocturnal hemoglobinuria (PNH)

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