Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Sort ascending Bone Marrow Disease
Efficacy and safety of luspatercept versus epoetin alfa in erythropoiesis-stimulating agent-naive, transfusion-dependent, lower-risk myelodysplastic syndromes (COMMANDS): interim analysis of a phase 3, open-label, randomised controlled trial Lancet Myelodysplastic Syndromes (MDS)
Progress in the Management of Pregnancy with Paroxysmal Nocturnal Hemoglobinuria: A Review Journal of Women's Health Paroxysmal Nocturnal Hemoglobinuria (PNH)
A Survey of Provider Practices for Diagnosis and Treatment of Pediatric Moderate Aplastic Anemia From the North American Pediatric Aplastic Anemia Consortium Journal of Pediatric Hematology/Oncology (JPHO) Aplastic Anemia
Romiplostim for Treatment of Children and Young Adults With Severe Aplastic Anemia and Myelodysplastic Syndrome Journal of Pediatric Hematology/Oncology Aplastic Anemia
Content validity of patient-reported outcomes for use in lower-risk myelodysplastic syndromes Journal of Patient-Reported Outcomes Myelodysplastic Syndromes (MDS)
Paroxysmal nocturnal hemoglobinuria: current treatments and unmet needs Journal of Managed care and specialty pharmacy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal nocturnal hemoglobinuria: patient journey and burden of disease Journal of Managed care and specialty pharmacy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal nocturnal hemoglobinuria: role of the complement system, pathogenesis, and pathophysiology Journal of Managed care and specialty pharmacy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Iptacopan and danicopan for paroxysmal nocturnal hemoglobinuria Journal of Managed Care & Specialty Pharmacy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Early transfusion patterns improve the Molecular International Prognostic Scoring System (IPSS-M) prediction in myelodysplastic syndromes Journal of Internal Medicine Myelodysplastic Syndromes (MDS)

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