Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Sort descending Bone Marrow Disease
Antithymocyte globulin and cyclosporin: standard of care also for older patients with aplastic anemia. Haematologica Aplastic Anemia
Terminal complement inhibition and control of hemolysis in patients with paroxysmal nocturnal hemoglobinuria who switched from high-dose eculizumab to ravulizumab: a phase IV, single-arm clinical trial Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Danicopan: an oral complement factor D inhibitor for paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Immunosuppressive therapy for severe aplastic anemia in children under the age of 3 years yields a high response rate: a North American collaborative study Haematologica Aplastic Anemia
To Target the Untargetable: Elucidation of Synergy of APR-246 and Azacitidine in TP53 Mutant Myelodysplastic Syndromes and Acute Myeloid Leukemia Haematologica Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Immunosuppression and Growth Factors for Severe Aplastic Anemia: New Data for Old Questions Haematologica Aplastic Anemia
Towards graft- versus-host disease-free alternative donor transplant platforms for patients with acquired aplastic anemia Haematologica Aplastic Anemia, Graft Versus Host Disease (GVHD)
Granulocyte transfusions in severe aplastic anemia Haematologica Aplastic Anemia
Detectable mutations precede late myeloid neoplasia in aplastic anemia Haematologica Aplastic Anemia

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