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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Guideline-based indicators for adult patients with myelodysplastic syndromes Aug 2020 Blood Advances Myelodysplastic Syndromes (MDS)
Venetoclax and Hypomethylating Agents (HMAs) Induce High Response Rates in MDS, Including Patients After HMA Therapy Failure Jul 2020 Blood Advances Myelodysplastic Syndromes (MDS)
Determinants of low health-related quality of life in patients with myelodysplastic syndromes: EUMDS Registry study Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Pegcetacoplan controls hemolysis in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Jun 2023 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Haploidentical BMT for severe aplastic anemia with intensive GVHD prophylaxis including posttransplant cyclophosphamide Apr 2020 Blood Advances Aplastic Anemia
A phase 3 randomized study of 5-azacitidine maintenance vs observation after transplant in high-risk AML and MDS patients Nov 2020 Blood Advances Myelodysplastic Syndromes (MDS)
Observation and treatment in DDX41-mutated acute myeloid leukemia and myelodysplastic syndrome Apr 2023 Blood Cancer Myelodysplastic Syndromes (MDS)
Frequency and perturbations of various peripheral blood cell populations before and after eculizumab treatment in paroxysmal nocturnal hemoglobinuria Mar 2021 Blood cells, molecules and diseases Paroxysmal Nocturnal Hemoglobinuria (PNH)
Do anemia treatments improve quality of life and physical function in patients with myelodysplastic syndromes (MDS)? A systematic review Jul 2023 Blood Reviews Myelodysplastic Syndromes (MDS)
Prognostication in myelodysplastic syndromes (neoplasms): Molecular risk stratification finally coming of age May 2023 Blood Reviews Myelodysplastic Syndromes (MDS)