Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Switching patients with PNH from pegcetacoplan to iptacopan: a case series Hematology. Paroxysmal Nocturnal Hemoglobinuria (PNH)
Allogeneic HSCT in Aplastic Anemia: Current Evidence, Controversies, and Practical Decision-Making American Journal of Hematology Aplastic Anemia
Clonal Dynamics of Hematopoiesis in Aplastic Anemia after Immunosuppression and Eltrombopag NEJM Evid Aplastic Anemia
Clonal Selection and Evolution after Treatment of Severe Aplastic Anemia NEJM Evid Aplastic Anemia
Real-World Effectiveness and Safety of Ravulizumab in Patients With Paroxysmal Nocturnal Hemoglobinuria: Evidence From the International PNH Registry American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
An Immune Dysfunction Signature Score Predicts Survival in MDS Patients: Insights From a Longitudinal, Multicenter Study Cancer Sci Myelodysplastic Syndromes (MDS)
Baseline IPSS-M vs pretransplant risk downstaging as prognostic determinants in MDS undergoing allogeneic transplantation Blood Advances Myelodysplastic Syndromes (MDS)
A novel approach to defining progression in MDS and precursor myeloid conditions in the MDS Natural History Study Blood Advances Myelodysplastic Syndromes (MDS)
Development and validation of the predictive aplastic score system (PASS): a simplified tool to diagnose acquired aplastic anemia in adults Leukemia Aplastic Anemia
Immunosuppressive therapy for severe aplastic anemia in children under the age of 3 years yields a high response rate: a North American collaborative study Haematologica Aplastic Anemia

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