diagnosis

Judy's Story of PNH - Always Moving Forward - 2025 Kansas City Patient and Family Conference

Thumbnail for video Watch Now

Topic(s)

Paroxysmal Nocturnal Hemoglobinuria (PNH)

Judy talks about her PNH journey from diagnosis, treatment decisions and moving forward.

PNH and Current Therapies - from the 2025 Kansas City Patient and Family Conference

Thumbnail for video Watch Now

Topic(s)

Paroxysmal Nocturnal Hemoglobinuria (PNH)

Presenter(s)

Srinivasa Reddy Sanikommu, MD

In this recording, Dr. Srinivasa Sanikommu discusses current thinking on PNH and therapies that are available to patients. Recording includes the question-and-answer session.

2025 Bone Marrow Failure Summit - Aplastic Anemia Expert Panel Discussion

Thumbnail for video Watch Now

Topic(s)

Aplastic Anemia

Presenter(s)

Bhavisha Patel, MD

Pedro Prata, MD, PhD

Tapan M. Kadia, MD

Zoe McQuilten, MD

Watch aplastic anemia experts at the 2025 AAMDSIF Bone Marrow Failure Summit translate and discuss the latest science to advance patient outcomes. This session is moderated by Emma Groarke, MD from the National Heart, Lung, and Blood Institute. Session Topics: Clonal dynamics…

Urge your Members of Congress to Reverse the 57% Cut to the Congressionally Directed Medical Research Program

Original Publication Date

April 14, 2025

Article Source

Take Action

Federal budget negotiations are already under way. April 15 marks the 30-Day anniversary of the enactment of the 57% cut to CDMRP including the elimination of all funding to Bone Marrow Failure Research. Every medical research program at CDMRP directly impacts the health and…

2025 San Francisco - Bay Area Patient and Family Conference

Read more about 2025 San Francisco - Bay Area Patient and Family Conference

Recorded Sessions:

Nutrition for Aplastic Anemia, MDS, or PNH

Managing PNH Treatments

Advances in Aplastic Anemia

Secondary AML - Webinar 2025

Thumbnail for video Watch Now

Topic(s)

Acute Myeloid Leukemia (AML)

In this webinar, Drs. Fadi Haddad and Jayastu Senapati discuss the diagnosis secondary AML from MDS, treatment options available to patients and symptom management.

TP53-Mutated Acute Myeloid Leukemia and Blast Phase Myeloproliferative Neoplasm: Distinct Mutation Leads to Poorer Prognosis

Original Publication Date

March 28, 2025

Article Source

External Web Content

ABSTRACT Patients with TP53 mutations in acute myeloid leukemia (AML) and blast phase myeloproliferative neoplasms (MPN-BP) experience similar poor clinical outcomes. A retrospective analysis of 39 patients with TP53 mutations (23 with AML and 16 with MPN-BP) revealed comparable…

Real-World Outcomes of Relapsed/Refractory Core-Binding Factor Acute Myeloid Leukemia: A COMMAND Registry Study

Original Publication Date

March 10, 2025

Article Source

External Web Content

To the Editor, Core-binding factor acute myeloid leukemia (CBF-AML) is characterized by the presence of inv(16)/t(16;16) or t(8;21) and is classified as favorable risk by the 2022 European LeukemiaNet (ELN) guidelines [1]. We have previously reported on outcomes of patients with…

Standardization of Bone Marrow Reporting for Myelodysplastic Syndromes/Neoplasms on Behalf of the International Consortium for Myelodysplastic Syndromes/Neoplasms

Original Publication Date

March 10, 2025

Article Source

External Web Content

Abstract Context.—: Standardized bone marrow reporting specifically for myelodysplastic syndromes/neoplasms (MDS) is currently lacking in the literature and much needed in practice. Objective.—: To propose a standardized approach to MDS evaluation in bone marrow specimens by (1)…

2025 Rockville Patient and Family Conference Session: PNH

Thumbnail for video Watch Now

Topic(s)

Paroxysmal Nocturnal Hemoglobinuria (PNH)

Presenter(s)

Bhumika Patel, MD

In this recording, Dr. Bhumika Patel discusses what is new in PNH and current treatment options available to patients.

Subscribe to diagnosis

Your Gift Today Changes Lives

diagnosis

Judy's Story of PNH - Always Moving Forward - 2025 Kansas City Patient and Family Conference

PNH and Current Therapies - from the 2025 Kansas City Patient and Family Conference

2025 Bone Marrow Failure Summit - Aplastic Anemia Expert Panel Discussion

Urge your Members of Congress to Reverse the 57% Cut to the Congressionally Directed Medical Research Program

2025 San Francisco - Bay Area Patient and Family Conference

Recorded Sessions:

Secondary AML - Webinar 2025

TP53-Mutated Acute Myeloid Leukemia and Blast Phase Myeloproliferative Neoplasm: Distinct Mutation Leads to Poorer Prognosis

Real-World Outcomes of Relapsed/Refractory Core-Binding Factor Acute Myeloid Leukemia: A COMMAND Registry Study

Standardization of Bone Marrow Reporting for Myelodysplastic Syndromes/Neoplasms on Behalf of the International Consortium for Myelodysplastic Syndromes/Neoplasms

2025 Rockville Patient and Family Conference Session: PNH

Website Feedback

Patient Helpline