2025 Boston Patient and Family Conference
Session Recordings Available:
Paroxysmal Nocturnal Hemoglobinuria (PNH)
EPYSQLI (SB12; Biosimilar to Reference Eculizumab) in Asian and Non-Asian Patients With Paroxysmal Nocturnal Hemoglobinuria: Subgroup Analysis of a Global Phase III Randomized Controlled Trial
Introduction: SB12 demonstrated equivalence to reference eculizumab eculizumab: Eculizumab (Soliris ®) is given as an IV into a vein at the doctor’s office or at a special cent
Thrombosis at Unusual Sites: Focus on Myeloproliferative Neoplasms and Paroxysmal Nocturnal Hemoglobinuria
Patients with thrombosis thrombosis: (throm-BOE-suss) A blood clot (thrombus) that develops and attaches to a blood vessel. at an unusual site will need to be explored for rare causes of
Patient-reported improvements in paroxysmal nocturnal hemoglobinuria treated with iptacopan from 2 phase 3 studies
Iptacopan Iptacopan: FABHALTA, a complement factor B inhibitor, is the first oral medication approved to treat adults with paroxysmal nocturnal hemoglobinuria (PNH). It was approved by the U.S.
Judy's Story of PNH - Always Moving Forward - 2025 Kansas City Patient and Family Conference
Topic(s)
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Judy talks about her PNH journey from diagnosis, treatment decisions and moving forward.
PNH and Current Therapies - from the 2025 Kansas City Patient and Family Conference
Topic(s)
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Presenter(s)
Srinivasa Reddy Sanikommu, MD
In this recording, Dr. Srinivasa Sanikommu discusses current thinking on PNH and therapies that are available to patients. Recording includes the question-and-answer session.
PNH Complications, from the 2025 Kansas City Patient and Family Conference
Topic(s)
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Presenter(s)
Srinivasa Reddy Sanikommu, MD
In this recording, Dr. Srinivasa Sanikommu discusses PNH complications that can impact a patient - extravascular hemolysis, intravascular hemolysis, Budd-Chiari Syndrome and blood clots. Recording includes the question-and-answer session.
Transplant and GVHD Session - 2025 Kansas City Patient and Family Conference
Topic(s)
Bone Marrow Transplant
In this recording, Dr. Anurag Singh discusses transplant and potentials complications such as GVHD and treatment options. Recording includes the question-and-answer session.