Paroxysmal Nocturnal Hemoglobinuria (PNH)

Managing PNH Complications Webinar

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Topic(s)
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Presenter(s)
Srinivasa Reddy Sanikommu, MD
In this webinar, Dr. Srinivasa Sanikommu discusses the management of PNH and complications experienced by patients.

What is PNH? Webinar

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Topic(s)
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Presenter(s)
Srinivasa Reddy Sanikommu, MD
In this webinar, Dr. Srinivasa Sanikommu discusses the diagnosis of PNH and current treatments available to patients.

Non-therapeutic Study: The purpose of a non-therapeutic study is to increase the understanding of a disease or condition through observation, data collection, or other methods. A non-therapeutic study does not provide treatment or intervention for participants. This type of research contributes to general knowledge that may benefit others in the future by improving treatment or developing new therapies. PLEDGE – Patients’ Long-term Experience on VOYDEYA (Danicopan): Gathering Evidence in the Real-World

Status
Recruiting
Study Date (Range)
-
Bone Marrow Disease(s)
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Age Group
18 years and older
The IRB-approved observational Phase IV PLEDGE study is set-up to collect real-world data on adult patients with Paroxysmal Nocturnal Hemoglobinuria (PNH) with symptomatic extravascular hemolysis who recently started VOYDEYATM (danicopan) as add-on treatment to ULTOMIRIS®…

Iptacopan Yields Meaningful Hemoglobin Improvements in Pretreated PNH Group

Original Publication Date
Article Source
External Web Content
Data from APPULSE-PNH may support oral iptacopan as a potentially practice-changing option in patients with paroxysmal nocturnal hemoglobinuria. "Results from APPULSE-PNH and previous trials establish oral iptacopan monotherapy as a potentially practice-changing treatment capable…

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