Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Sort ascending Original Publication Date Journal Bone Marrow Disease
Oral decitabine cedazuridine with and without venetoclax in higher-risk myelodysplastic syndromes or chronic myelomonocytic leukemia: a propensity score-matched study Blood Cancer Journal Myelodysplastic Syndromes (MDS)
Oral complement factor D inhibitor danicopan for paroxysmal nocturnal hemoglobinuria Expert Review of Clinical Pharmacology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Optimal timing of allogeneic hematopoietic stem cell transplant in MDS Leukemia & Lymphoma Myelodysplastic Syndromes (MDS)
One-year outcomes from a phase 3 randomized trial of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria who received prior eculizumab European Journal of Haematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
One-year efficacy and safety of ravulizumab in adults with paroxysmal nocturnal hemoglobinuria naïve to complement inhibitor therapy: open-label extension of a randomized study Therapeutic Advances in Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Observation and treatment in DDX41-mutated acute myeloid leukemia and myelodysplastic syndrome Blood Cancer Myelodysplastic Syndromes (MDS)
Novel therapeutic choices in immune aplastic anemia F1000Research Aplastic Anemia
Novel targeted C3 inhibitor pegcetacoplan for paroxysmal nocturnal hemoglobinuria Clinical and Experimental Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Novel Approaches and Future Directions in Myelodysplastic Syndrome Treatment The Cancer Journal Myelodysplastic Syndromes (MDS)
Newly revised 2023 MDS response criteria Blood Myelodysplastic Syndromes (MDS)

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