Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Sort ascending Bone Marrow Disease
Pegcetacoplan controls hemolysis in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
An agenda to advance research in myelodysplastic syndromes: a TOP 10 priority list from the first international workshop in MDS Blood Advances Myelodysplastic Syndromes (MDS)
Discordant pathologic diagnoses of myelodysplastic neoplasms and their implications for registries and therapies Blood Advances Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS), Myeloproliferative Neoplasms (MPN)
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Guideline-based indicators for adult patients with myelodysplastic syndromes Blood Advances Myelodysplastic Syndromes (MDS)
Towards a Conceptualization of Measurable Residual Disease in Myelodysplastic Syndromes Blood Advances Myelodysplastic Syndromes (MDS)
Impact of HLA alloimmunization on clinical outcomes of severe aplastic anemia treated with immunosuppressive therapy Blood Advances Aplastic Anemia
Statin Use in Myelodysplastic Syndromes Is Associated with a Better Survival and Decreased Progression to Leukemia Blood Advances Myelodysplastic Syndromes (MDS)
Activity of luspatercept and ESAs combination for treatment of anemia in lower-risk myelodysplastic syndromes Blood Advances Myelodysplastic Syndromes (MDS)
Determinants of low health-related quality of life in patients with myelodysplastic syndromes: EUMDS Registry study Blood Advances Myelodysplastic Syndromes (MDS)

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