Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Sort ascending Bone Marrow Disease
Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Granulocyte transfusions in severe aplastic anemia Haematologica Aplastic Anemia
Terminal complement inhibition and control of hemolysis in patients with paroxysmal nocturnal hemoglobinuria who switched from high-dose eculizumab to ravulizumab: a phase IV, single-arm clinical trial Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Immunosuppressive therapy for pediatric aplastic anemia: a North American Pediatric Aplastic Anemia Consortium study Haematologica Aplastic Anemia
Characterization of breakthrough hemolysis events observed in the phase 3 randomized studies of ravulizumab versus eculizumab in adults with paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Time without transfusion reliance: a novel patient-centric metric for new therapies in myelodysplastic syndromes Haematologica Myelodysplastic Syndromes (MDS)
Current use of androgens in bone marrow failure disorders: a report from the Severe Aplastic Anemia Working Party of the European Society for Blood and Marrow Transplantation Haematologica Aplastic Anemia
Is blood transfusion safe during the COVID-19 pandemic? Future Science OA Aplastic Anemia, Myelodysplastic Syndromes (MDS), Paroxysmal Nocturnal Hemoglobinuria (PNH)
Luspatercept in the treatment of lower-risk myelodysplastic syndromes Future Oncology (London, England) Myelodysplastic Syndromes (MDS)
Targeting the Microenvironment in MDS: The Final Frontier Frontiers in Pharmacology Myelodysplastic Syndromes (MDS)

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