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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Cost-effectiveness of iptacopan for paroxysmal nocturnal hemoglobinuria Oct 2024 Blood Paroxysmal Nocturnal Hemoglobinuria (PNH)
Discordant pathologic diagnoses of myelodysplastic neoplasms and their implications for registries and therapies Oct 2023 Blood Advances Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS), Myeloproliferative Neoplasms (MPN)
Towards a Conceptualization of Measurable Residual Disease in Myelodysplastic Syndromes Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Consensus recommendations for severe aplastic anemia Nov 2024 Blood Advances Aplastic Anemia
Guideline-based indicators for adult patients with myelodysplastic syndromes Aug 2020 Blood Advances Myelodysplastic Syndromes (MDS)
Venetoclax and Hypomethylating Agents (HMAs) Induce High Response Rates in MDS, Including Patients After HMA Therapy Failure Jul 2020 Blood Advances Myelodysplastic Syndromes (MDS)
Determinants of low health-related quality of life in patients with myelodysplastic syndromes: EUMDS Registry study Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Consensus Recommendations for Severe Aplastic Anemia Aug 2024 Blood Advances Aplastic Anemia
Hemolysis events in the Phase 3 PEGASUS study of pegcetacoplan in patients with paroxysmal nocturnal hemoglobinuria Apr 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Modified Delphi panel consensus recommendations for management of severe aplastic anemia Aug 2024 Blood Advances Aplastic Anemia