Research Articles | Aplastic Anemia and MDS International Foundation (AAMDSIF) Return to top.

Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study Apr 2024 Advances in Therapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Complement Inhibition in Paroxysmal Nocturnal Hemoglobinuria (PNH): A Systematic Review and Expert Opinion from Central Europe on Special Patient Populations Jun 2023 Advances in Therapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
HDAC4 inhibition disrupts TET2 function in high-risk MDS and AML Jul 2020 Aging Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Calculator-free point-of-care prognostication in myelodysplastic syndromes. Jan 2019 Am J Hematol Myelodysplastic Syndromes (MDS)
Effectiveness of eculizumab in patients with paroxysmal nocturnal hemoglobinuria (PNH) with or without aplastic anemia in the International PNH Registry Jan 2019 Am J Hematol Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH)
How I Diagnose Low-Grade Myelodysplastic Syndromes May 2020 American Journal of clinical Pathology Myelodysplastic Syndromes (MDS)
Paroxysmal nocturnal hemoglobinuria: Where we stand May 2023 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal nocturnal hemoglobinuria: Where are we going May 2023 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Distinct and convergent consequences of splice factor mutations in myelodysplastic syndromes Nov 2019 American Journal of Hematology Myelodysplastic Syndromes (MDS)
Iron overload after complement inhibitor treatment of Paroxysmal Nocturnal Hemoglobinuria Apr 2021 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)