Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Sort descending Journal Bone Marrow Disease
Efficacy and safety of the C5 inhibitor crovalimab in complement inhibitor-naive patients with PNH (COMMODORE 3): A multicenter, Phase 3, single-arm study American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Factor B inhibitor iptacopan for the treatment of paroxysmal nocturnal hemoglobinuria Blood Reviews Paroxysmal Nocturnal Hemoglobinuria (PNH)
Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
A Journey from Blood Cells to Genes and Back Annual Review of Genomics and Human Genetics Paroxysmal Nocturnal Hemoglobinuria (PNH)
Eltrombopag for Low-Risk Myelodysplastic Syndromes With Thrombocytopenia: Interim Results of a Phase II, Randomized, Placebo-Controlled Clinical Trial (EQOL-MDS) Journal of Clinical Oncology Myelodysplastic Syndromes (MDS)
Patterns of Diagnostic Evaluation and Determinants of Treatment in Older Patients With Non-transfusion Dependent Myelodysplastic Syndromes Oncologist Myelodysplastic Syndromes (MDS)
Deciphering treatment patterns in non-severe/moderate aplastic anemia: an international observational study Leukemia Aplastic Anemia
Predictors for improvement in patient-reported outcomes: post hoc analysis of a phase 3 randomized, open-label study of eculizumab and ravulizumab in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Clonal Hematopoiesis, Inflammation, and Hematologic Malignancy Annual Review of Pathology: Mechanisms of Disease Aplastic Anemia, Myelodysplastic Syndromes (MDS), Paroxysmal Nocturnal Hemoglobinuria (PNH)
Clinical decision‐making and treatment of myelodysplastic syndromes Blood Myelodysplastic Syndromes (MDS)

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