Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Sort ascending Original Publication Date Journal Bone Marrow Disease
Safety and Efficacy of Pegcetacoplan in Adult Patients with Paroxysmal Nocturnal Hemoglobinuria over 48 Weeks: 307 Open-Label Extension Study Advances in Therapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
Safety and efficacy of danicopan in patients with paroxysmal nocturnal hemoglobinuria: a systematic review and meta-analysis Expert Review of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Safety and activity of selinexor in patients with myelodysplastic syndromes or oligoblastic acute myeloid leukaemia refractory to hypomethylating agents: a single-centre, single-arm, phase 2 trial Lancet Hematology Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Sabatolimab plus hypomethylating agents in previously untreated patients with higher-risk myelodysplastic syndromes (STIMULUS-MDS1): a randomised, double-blind, placebo-controlled, phase 2 trial Lancet Hematology Myelodysplastic Syndromes (MDS)
Romiplostim for Treatment of Children and Young Adults With Severe Aplastic Anemia and Myelodysplastic Syndrome Journal of Pediatric Hematology/Oncology Aplastic Anemia
Romiplostim for aplastic anemia: beyond an eltrombopag alternative. Haematologica Aplastic Anemia
Role of innate immunological/inflammatory pathways in myelodysplastic syndromes and AML: a narrative review Experimental Hematology & Oncology Myelodysplastic Syndromes (MDS)
RNA splicing as a therapeutic target in myelodysplastic syndromes Seminars in Hematology Myelodysplastic Syndromes (MDS)
Risk-Adapted, Individualized Treatment Strategies of Myelodysplastic Syndromes (MDS) and Chronic Myelomonocytic Leukemia (CMML) Cancers Chronic Myelomonocytic Leukaemia (CMML), Myelodysplastic Syndromes (MDS)
Risk factors for de novo and therapy-related myelodysplastic syndromes (MDS) Cancer Causes & Control : CCC Myelodysplastic Syndromes (MDS)

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