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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
What are the most important quality of life domains for patients with aplastic anemia and paroxysmal nocturnal hemoglobinuria? May 2025 Annals of Hematology Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH)
Towards graft- versus-host disease-free alternative donor transplant platforms for patients with acquired aplastic anemia May 2025 Haematologica Aplastic Anemia, Graft Versus Host Disease (GVHD)
The Advancing Landscape of Paroxysmal Nocturnal Hemoglobinuria Treatment May 2025 Turkish Journal of Haematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Disease Burden at the Time of Transplantation Is a Primary Predictor of Outcomes in Pediatric MDS: A Single-Center Experience May 2025 Cancers Myelodysplastic Syndromes (MDS), Pediatric
New Approvals in Low- and Intermediate-Risk Myelodysplastic Syndromes May 2025 American Society of Clinical Oncology Educational Book Myelodysplastic Syndromes (MDS)
Thrombosis at Unusual Sites: Focus on Myeloproliferative Neoplasms and Paroxysmal Nocturnal Hemoglobinuria Apr 2025 Hamostaseologie Myeloproliferative Neoplasms (MPN), Paroxysmal Nocturnal Hemoglobinuria (PNH)
Elderly Patients With Aplastic Anemia: Treatment Patterns and Outcomes in the Real World Apr 2025 American Journal of Hematology Aplastic Anemia
Initial management of patients with acquired aplastic anemia in the United States: results from a large national claims database Apr 2025 Annals of Hematology Aplastic Anemia
Patient-reported improvements in paroxysmal nocturnal hemoglobinuria treated with iptacopan from 2 phase 3 studies Apr 2025 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Infections in lower-risk myelodysplastic syndromes - prevalence and risk factors: a report from the European MDS Registry Apr 2025 Haematologica Myelodysplastic Syndromes (MDS)