Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Sort descending Bone Marrow Disease
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Towards a Conceptualization of Measurable Residual Disease in Myelodysplastic Syndromes Blood Advances Myelodysplastic Syndromes (MDS)
Determinants of low health-related quality of life in patients with myelodysplastic syndromes: EUMDS Registry study Blood Advances Myelodysplastic Syndromes (MDS)
Transplantation in patients with lower-risk MDS: a prospective phase 2 trial based on donor availability Blood Advances Myelodysplastic Syndromes (MDS)
Health-Related Quality of Life and Vulnerability among People with Myelodysplastic Syndromes: A US National Study Blood Advances Myelodysplastic Syndromes (MDS)
Consensus Recommendations for Severe Aplastic Anemia Blood Advances Aplastic Anemia
Venetoclax and Hypomethylating Agents (HMAs) Induce High Response Rates in MDS, Including Patients After HMA Therapy Failure Blood Advances Myelodysplastic Syndromes (MDS)
Modified Delphi panel consensus recommendations for management of severe aplastic anemia Blood Advances Aplastic Anemia
Patient-reported improvements in paroxysmal nocturnal hemoglobinuria treated with iptacopan from 2 phase 3 studies Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Hemolysis events in the Phase 3 PEGASUS study of pegcetacoplan in patients with paroxysmal nocturnal hemoglobinuria Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)

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