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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Acquired Aplastic Anemia: What Have We Learned and What Is in the Horizon? Jun 2018 Pediatr Clin North Am. aplastic anemia
Acquired aplastic anemia in children Oct 2013 Pediatr Clin North Am aplastic anemia
Pilot trial of risk-adapted cyclophosphamide intensity based conditioning and HLA matched sibling and unrelated cord blood stem cell transplantation in newly diagnosed pediatric and adolescent recipients with acquired severe aplastic anemia Feb 2014 Pediatr Blood Cancer aplastic anemia
Efficacy and safety of eculizumab in children and adolescents with paroxysmal nocturnal hemoglobinuria Apr 2014 Pediatr Blood Cancer paroxysmal nocturnal hemoglobinuria (PNH)
Long-term outcomes of 95 children with moderate aplastic anemia treated with horse antithymocyte globulin and cyclosporine Nov 2016 Pediatr Blood Cancer aplastic anemia
Immune markers of disease severity and treatment response in pediatric acquired aplastic anemia Jul 2012 Pediatr Blood Cancer aplastic anemia
Outcomes and healthcare utilization in children and young adults with aplastic anemia: A multiinstitutional analysis Jul 2017 Pediatr Blood Cancer aplastic anemia
Eculizumab treatment of paroxysmal nocturnal hemoglobinuria presenting as moyamoya syndrome in a 9-year-old male. Jan 2012 Pediatr Blood Cancer paroxysmal nocturnal hemoglobinuria (PNH)
Diagnosis and treatment of pediatric acquired aplastic anemia (AAA): An initial survey of the North American Pediatric Aplastic Anemia Consortium (NAPAAC) Nov 2013 Pediatr Blood Cancer aplastic anemia
Myelodysplastic Syndromes Treatment (PDQ®): Patient Version Oct 2015 PDQ Cancer Information Summaries [Internet] myelodysplastic syndromes (MDS)
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