Drugs | Page 3 | Aplastic Anemia & MDS International Foundation


More drugs are available to treat bone marrow failure disease than ever before. Researchers constantly look for ways to enhance drugs already on the market and develop new ones with fewer side effects. Some drugs treat only one type of the disease, while others may be used to treat more than one type. Check with your doctor to find out which drugs are right for you and why.

Mycophenolate Mofetil

Brand Name: CellCept
Treatment for: aplastic anemia
A drug that lowers the body's immune response, also referred to as an immunosuppressant drug.


Brand Name: Ultomiris®
Treatment for: paroxysmal nocturnal hemoglobinuria (PNH)


Brand Name: Prograf
Treatment for: aplastic anemia


Brand Name: Thalomid
Treatment for: myelodysplastic syndromes (MDS)
Thalidomide is an old drug, though it has not been widely available since the 1960s, when it was found to cause birth defects.


Brand Name: Coumadin
Treatment for:
A blood thinner, or anticoagulant.

AAMDSIF does not recommend, endorse, or make any representation about the efficacy, appropriateness or suitability of any drug, treatment or therapy listed on this website. Some therapies listed on our site are considered experimental for the treatment of bone marrow failure diseases. Always seek the advice of your physician or other qualified health care provider with any questions you may have regarding any therapy, and never disregard professional medical advice or delay in seeking it because of something you have read on this website.