Presentation materials from the 2019 AAMDSIF Patient & Family Conference in St. Louis, Missouri.
Johnnie Burford was deployed in Korea. He was a muscular 195-lb athlete, a proud member of the US Army Second Division. Nothing stopped him from performing his duty. Yet a rapid weight loss of 100 pounds, coupled with unusual bruising, alerted him that something was very wrong.
People with severe
This is a phase II, open label, multi-center, intra-patient dose escalation study to characterize the pharmacokinetics after oral administration of
Conference materials from the 2019 Patient & Family Conference: Pittsburgh area
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