Know Your Treatment Options

Because you play a critical role in how well treatment works for you, you need to learn all you can about your disease and the available treatments for it. This overview of treatment options for aplastic anemia, MDS and PNH will get you started and direct you to where you can learn more.

Caring for Yourself

We help you cope with your battle against bone marrow failure disease. Much of the information we provide teaches patients and families how to be proactive members of their health care team. Patients just like you have also learned how to develop their inner strength by connecting with our community and taking advantage of our resources.

 

Therapies

There are many therapies and approaches doctors use to treat bone marrow failure disease patients. Some treatments are used for several different diseases. Others are used only for aplastic anemia, MDS or PNH. Every person's condition is unique, and each situation is different. That's why your health care team must look carefully at your specific case before recommending what's right for you.

 

Bone Marrow Transplants

A bone marrow transplant (BMT) is also called a stem cell transplant (SCT) or hematopoietic stem cell transplant (HSCT).The procedure replaces unhealthy blood-forming stem cells with healthy ones and offers some patients the possibility of a cure. But for many patients, a BMT is not an option due to the risks and potential long-term side effects as an "imperfect cure".

 

Clinical Trials

Clinical research is at the heart of all medical advances, identifying new ways to prevent, detect or treat disease. If you have a bone marrow failure disease, you may want to consider taking part in a clinical trial, also called a research study.

 

Drugs

More drugs are available to treat bone marrow failure disease than ever before. Researchers constantly look for ways to enhance drugs already on the market and develop new ones with fewer side effects. Some drugs treat only one type of the disease, while others may be used to treat more than one type. Check with your doctor to find out which drugs are right for you and why.