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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Complement Inhibition in Paroxysmal Nocturnal Hemoglobinuria (PNH): A Systematic Review and Expert Opinion from Central Europe on Special Patient Populations Jun 2023 Advances in Therapy Paroxysmal Nocturnal Hemoglobinuria (PNH)
HDAC4 inhibition disrupts TET2 function in high-risk MDS and AML Jul 2020 Aging Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Calculator-free point-of-care prognostication in myelodysplastic syndromes. Jan 2019 Am J Hematol Myelodysplastic Syndromes (MDS)
Effectiveness of eculizumab in patients with paroxysmal nocturnal hemoglobinuria (PNH) with or without aplastic anemia in the International PNH Registry Jan 2019 Am J Hematol Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH)
How I Diagnose Low-Grade Myelodysplastic Syndromes May 2020 American Journal of clinical Pathology Myelodysplastic Syndromes (MDS)
Paroxysmal nocturnal hemoglobinuria: Where we stand May 2023 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Paroxysmal nocturnal hemoglobinuria: Where are we going May 2023 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Iron overload after complement inhibitor treatment of Paroxysmal Nocturnal Hemoglobinuria Apr 2021 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Myelodysplastic Syndromes: 2021 update on Diagnosis, Risk-stratification and Management Aug 2020 American Journal of Hematology Myelodysplastic Syndromes (MDS)
Alemtuzumab in relapsed immune severe aplastic anemia: Long-term results of a phase II study Apr 2023 American Journal of Hematology Aplastic Anemia