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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Effectiveness and safety of tacrolimus with or without eltrombopag, as a part of immunosuppressive treatment of aplastic anemia in adults: a retrospective case series Jan 2021 Annals of Hematology Aplastic Anemia
Baseline Clinical Characteristics and Disease Burden in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH): Updated Analysis From the International PNH Registry May 2020 Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Predictors for improvement in patient-reported outcomes: post hoc analysis of a phase 3 randomized, open-label study of eculizumab and ravulizumab in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Oct 2023 Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Development of a target concentration intervention to individualize paroxysmal nocturnal hemoglobinuria treatment with pegcetacoplan Jul 2024 Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
The prognostic value of serum erythropoietin in patients with lower-risk myelodysplastic syndromes: a review of the literature and expert opinion Oct 2019 Annals of Hematology Myelodysplastic Syndromes (MDS)
New Approvals in Low- and Intermediate-Risk Myelodysplastic Syndromes May 2025 American Society of Clinical Oncology Educational Book Myelodysplastic Syndromes (MDS)
New Approvals in Low- and Intermediate-Risk Myelodysplastic Syndromes Jun 2025 American Society of Clinical Oncology Educational Book Myelodysplastic Syndromes (MDS)
Haploidentical stem cell transplantation (haplo-SCT) represents the main alternative for children with inherited bone marrow failure syndrome (I-BMF) lacking a matched donor. This retrospective study, conducted on behalf of the EBMT SAAWP and PDWP, aims t Jun 2024 American Society of Clinical Oncology Educational Book Myelodysplastic Syndromes (MDS)
Myelodysplastic syndromes with ring sideroblasts (MDS-RS) and MDS/myeloproliferative neoplasm with RS and thrombocytosis (MDS/MPN-RS-T) - "2021 update on diagnosis, risk-stratification, and management" Jan 2021 American Journal of Hematology Myelodysplastic Syndromes (MDS), Myeloproliferative Neoplasms (MPN)
Massive hemolysis in paroxysmal nocturnal hemoglobinuria after switching from proximal complement inhibitor to anti-C5 therapy: A lesson not to be forgotten Oct 2024 American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)