Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Sort ascending Bone Marrow Disease
Understanding pharmacological complement inhibition in paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Hematopoietic stem cell transplantation is effective in achieving long-term survival for post-aplastic anemia myeloid neoplasms: the EBMT Severe Aplastic Anemia Report Haematologica Aplastic Anemia
Conditional survival and standardized mortality ratios of patients with severe aplastic anemia surviving at least one year after hematopoietic cell transplantation or immunosuppressive therapy Haematologica Aplastic Anemia
Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Terminal complement inhibition and control of hemolysis in patients with paroxysmal nocturnal hemoglobinuria who switched from high-dose eculizumab to ravulizumab: a phase IV, single-arm clinical trial Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Immunosuppressive therapy for severe aplastic anemia in children under the age of 3 years yields a high response rate: a North American collaborative study Haematologica Aplastic Anemia
Granulocyte transfusions in severe aplastic anemia Haematologica Aplastic Anemia
To Target the Untargetable: Elucidation of Synergy of APR-246 and Azacitidine in TP53 Mutant Myelodysplastic Syndromes and Acute Myeloid Leukemia Haematologica Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Infections in lower-risk myelodysplastic syndromes - prevalence and risk factors: a report from the European MDS Registry Haematologica Myelodysplastic Syndromes (MDS)
Time without transfusion reliance: a novel patient-centric metric for new therapies in myelodysplastic syndromes Haematologica Myelodysplastic Syndromes (MDS)

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