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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Similar outcomes of alemtuzumab-based hematopoietic cell transplantation for SAA patients older or younger than 50 years Oct 2019 Blood Advances Aplastic Anemia
Long-term efficacy and safety of romiplostim in refractory aplastic anemia: follow-up of a phase 2/3 study Dec 2023 Blood Advances Aplastic Anemia
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Jun 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
DNA methylation identifies genetically and prognostically distinct subtypes of myelodysplastic syndromes Oct 2019 Blood Advances Myelodysplastic Syndromes (MDS)
A phase 3 randomized study of 5-azacitidine maintenance vs observation after transplant in high-risk AML and MDS patients Nov 2020 Blood Advances Myelodysplastic Syndromes (MDS)
Activity of luspatercept and ESAs combination for treatment of anemia in lower-risk myelodysplastic syndromes Jul 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Outpatient subcutaneous alemtuzumab is feasible and safe for aplastic anemia and is associated with high response rates Feb 2025 Blood Advances Aplastic Anemia
Health-related quality of life and vulnerability among people with myelodysplastic syndromes: a US national study Jul 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Pegcetacoplan controls hemolysis in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Jun 2023 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Why do we not have more drugs approved for MDS? A critical viewpoint on novel drug development in MDS Jul 2023 Blood Advances Myelodysplastic Syndromes (MDS)