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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Cost-effectiveness of iptacopan for paroxysmal nocturnal hemoglobinuria Oct 2024 Blood Paroxysmal Nocturnal Hemoglobinuria (PNH)
Glasdegib as maintenance therapy for patients with AML and MDS patients at high risk for postallogeneic stem cell transplant relapse Jul 2020 Blood Advances Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS)
Consensus recommendations for severe aplastic anemia Nov 2024 Blood Advances Aplastic Anemia
A genomics-informed computational biology platform prospectively predicts treatment responses in AML and MDS patients Jun 2019 Blood Advances Myelodysplastic Syndromes (MDS)
An agenda to advance research in myelodysplastic syndromes: a TOP 10 priority list from the first international workshop in MDS Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Consensus Recommendations for Severe Aplastic Anemia Aug 2024 Blood Advances Aplastic Anemia
Haploidentical BMT for severe aplastic anemia with intensive GVHD prophylaxis including posttransplant cyclophosphamide Apr 2020 Blood Advances Aplastic Anemia
Modified Delphi panel consensus recommendations for management of severe aplastic anemia Aug 2024 Blood Advances Aplastic Anemia
Discordant pathologic diagnoses of myelodysplastic neoplasms and their implications for registries and therapies Oct 2023 Blood Advances Acute Myeloid Leukemia (AML), Myelodysplastic Syndromes (MDS), Myeloproliferative Neoplasms (MPN)
Towards a Conceptualization of Measurable Residual Disease in Myelodysplastic Syndromes Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)