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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Outcomes of pediatric patients who relapse after first HCT for acute leukemia or MDS Mar 2021 Bone Marrow Transplantation Myelodysplastic Syndromes (MDS)
Outcome of lower-risk myelodysplastic syndrome with ring sideroblasts (MDS-RS) after failure of erythropoiesis- stimulating agents Dec 2020 Leukemia Research Myelodysplastic Syndromes (MDS)
Oral therapy for myelodysplastic syndromes/neoplasms and acute myeloid leukemia: a revolution in progress Jul 2023 Expert Review of Anticancer Therapies Myelodysplastic Syndromes (MDS)
Oral Iptacopan Monotherapy in Paroxysmal Nocturnal Hemoglobinuria Mar 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria. Reply Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral Iptacopan in Paroxysmal Nocturnal Hemoglobinuria Jun 2024 The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Oral decitabine-cedazuridine versus intravenous decitabine for myelodysplastic syndromes and chronic myelomonocytic leukaemia (ASCERTAIN): a registrational, randomised, crossover, pharmacokinetics, phase 3 study Jan 2024 Lancet Hematology Myelodysplastic Syndromes (MDS)
Oral decitabine cedazuridine with and without venetoclax in higher-risk myelodysplastic syndromes or chronic myelomonocytic leukemia: a propensity score-matched study Mar 2025 Blood Cancer Journal Myelodysplastic Syndromes (MDS)
Oral complement factor D inhibitor danicopan for paroxysmal nocturnal hemoglobinuria Sep 2024 Expert Review of Clinical Pharmacology Paroxysmal Nocturnal Hemoglobinuria (PNH)