Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Sort ascending Original Publication Date Journal Bone Marrow Disease
Phase 2 Study of the ALK5 Inhibitor Galunisertib in Very Low-, Low-, and Intermediate-Risk Myelodysplastic Syndromes Clinical Cancer Research: an official Journal of the American Association of Cancer Research Myelodysplastic Syndromes (MDS)
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pegcetacoplan: the first and only C3-targeted therapy for the treatment of adults with paroxysmal nocturnal hemoglobinuria Expert Review of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pegcetacoplan versus Eculizumab in Paroxysmal Nocturnal Hemoglobinuria The New England Journal of Medicine Paroxysmal Nocturnal Hemoglobinuria (PNH)
Pegcetacoplan controls hemolysis in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Patterns of Diagnostic Evaluation and Determinants of Treatment in Older Patients With Non-transfusion Dependent Myelodysplastic Syndromes The Oncologist Myelodysplastic Syndromes (MDS)
Patterns of Diagnostic Evaluation and Determinants of Treatment in Older Patients With Non-transfusion Dependent Myelodysplastic Syndromes The Oncologist Myelodysplastic Syndromes (MDS)
Patterns of Diagnostic Evaluation and Determinants of Treatment in Older Patients With Non-transfusion Dependent Myelodysplastic Syndromes Oncologist Myelodysplastic Syndromes (MDS)
Patients' perspectives on oral decitabine/cedazuridine for the treatment of myelodysplastic syndromes/neoplasms Therapeutic Advances in Hematology Myelodysplastic Syndromes (MDS)
Patients with paroxysmal nocturnal hemoglobinuria demonstrate a prothrombotic clotting phenotype which is improved by complement inhibition with eculizumab American Journal of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)

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