Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Sort ascending Bone Marrow Disease
Baseline Clinical Characteristics and Disease Burden in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH): Updated Analysis From the International PNH Registry Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Initial management of patients with acquired aplastic anemia in the United States: results from a large national claims database Annals of Hematology Aplastic Anemia
What are the most important quality of life domains for patients with aplastic anemia and paroxysmal nocturnal hemoglobinuria? Annals of Hematology Aplastic Anemia, Paroxysmal Nocturnal Hemoglobinuria (PNH)
Health-related quality of life and symptom-specific functional impairment among patients treated with parenterally administered complement inhibitors for paroxysmal nocturnal hemoglobinuria Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Patient-reported outcomes in patients with paroxysmal nocturnal hemoglobinuria treated with crovalimab and approved C5 inhibitors in the phase III COMMODORE 2 and 1 studies Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Predictors for improvement in patient-reported outcomes: post hoc analysis of a phase 3 randomized, open-label study of eculizumab and ravulizumab in complement inhibitor-naive patients with paroxysmal nocturnal hemoglobinuria Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
Evolving therapies for lower-risk myelodysplastic syndromes Annals of Hematology Myelodysplastic Syndromes (MDS)
Baseline Clinical Characteristics and Disease Burden in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH): Updated Analysis From the International PNH Registry Annals of Hematology Paroxysmal Nocturnal Hemoglobinuria (PNH)
New Approvals in Low- and Intermediate-Risk Myelodysplastic Syndromes American Society of Clinical Oncology Educational Book Myelodysplastic Syndromes (MDS)
Haploidentical stem cell transplantation (haplo-SCT) represents the main alternative for children with inherited bone marrow failure syndrome (I-BMF) lacking a matched donor. This retrospective study, conducted on behalf of the EBMT SAAWP and PDWP, aims t American Society of Clinical Oncology Educational Book Myelodysplastic Syndromes (MDS)

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