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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Consensus recommendations for severe aplastic anemia Nov 2024 Blood Advances Aplastic Anemia
Health-related quality of life and vulnerability among people with myelodysplastic syndromes: a US national study Jul 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Patient-reported improvements in paroxysmal nocturnal hemoglobinuria treated with iptacopan from 2 phase 3 studies Apr 2025 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Why do we not have more drugs approved for MDS? A critical viewpoint on novel drug development in MDS Jul 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Consensus Recommendations for Severe Aplastic Anemia Aug 2024 Blood Advances Aplastic Anemia
Modified Delphi panel consensus recommendations for management of severe aplastic anemia Aug 2024 Blood Advances Aplastic Anemia
Health-Related Quality of Life and Vulnerability among People with Myelodysplastic Syndromes: A US National Study May 2023 Blood Advances Myelodysplastic Syndromes (MDS)
An agenda to advance research in myelodysplastic syndromes: a TOP 10 priority list from the first international workshop in MDS Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)
Pharmacokinetics, pharmacodynamics, efficacy, and safety of ravulizumab in pediatric paroxysmal nocturnal hemoglobinuria Jun 2024 Blood Advances Paroxysmal Nocturnal Hemoglobinuria (PNH)
Towards a Conceptualization of Measurable Residual Disease in Myelodysplastic Syndromes Jun 2023 Blood Advances Myelodysplastic Syndromes (MDS)