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Research Articles

Compiled for your convenience are articles on bone marrow failure research and treatment from the world’s major journals on hematology / oncology.

Article Title Original Publication Date Journal Bone Marrow Disease
Granulocyte transfusions in severe aplastic anemia Dec 2023 Haematologica Aplastic Anemia
Characterization of breakthrough hemolysis events observed in the phase 3 randomized studies of ravulizumab versus eculizumab in adults with paroxysmal nocturnal hemoglobinuria Jan 2020 Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Danicopan: an oral complement factor D inhibitor for paroxysmal nocturnal hemoglobinuria Oct 2020 Haematologica Paroxysmal Nocturnal Hemoglobinuria (PNH)
Detectable mutations precede late myeloid neoplasia in aplastic anemia Feb 2021 Haematologica Aplastic Anemia
Is blood transfusion safe during the COVID-19 pandemic? Sep 2020 Future Science OA Aplastic Anemia, Myelodysplastic Syndromes (MDS), Paroxysmal Nocturnal Hemoglobinuria (PNH)
Luspatercept in the treatment of lower-risk myelodysplastic syndromes Jan 2021 Future Oncology (London, England) Myelodysplastic Syndromes (MDS)
Targeting the Microenvironment in MDS: The Final Frontier Jul 2020 Frontiers in Pharmacology Myelodysplastic Syndromes (MDS)
The role of androgen therapy in acquired aplastic anemia and other bone marrow failure syndromes May 2023 Frontiers in Oncology Aplastic Anemia
Novel therapeutic choices in immune aplastic anemia Sep 2020 F1000Research Aplastic Anemia
Management of aplastic anemia after failure of frontline immunosuppression Jul 2019 Expert Review of Hematology Aplastic Anemia